Opportunities in a Wide Array of Genetic DiseasesWith the versatility of genetic cargo and flexibility in administration, ReCode’s SORT LNP technology has potential applications across many genetically defined conditions, including muscular, CNS, liver, infectious disease and oncology indications.
(PCD) mRNA DNAI1 Inhaled
(CF) mRNA CFTR Inhaled
Alpha-1 antitrypsin Gene correction SERPINA1 Inhaled
cns Various Multiple Undisclosed Intrathecal