Media Contact
The Grace Communication Group
Tara Cooper
[email protected]
[email protected]
Investor Contact
Stern IR
Sarah McCabe
[email protected]
[email protected]
Press Releases
Presentations
Rescue of Ciliary Function in Primary Ciliary Dyskinesia using Nebulized LNP-formulated DNAI1 mRNA
October 4, 2022
5th European Cilia Conference
Functional Rescue of CFTR by Aerosolized Delivery of Optimized CFTR mRNA Using ReCode LNPs in Primary Human Bronchial Epithelial Cells Derived From Patients With Cystic Fibrosis
May 18, 2022
American Thoracic Society (ATS) 2022 International Conference
An mRNA-Based Therapy to Treat Primary Ciliary Dyskinesia: Aerosol Delivery, Biodistribution and Tolerability
May 15, 2022
American Thoracic Society (ATS) 2022 International Conference
Optimization of DNAI1 mRNA Constructs to Treat Primary Ciliary Dyskinesia
May 15, 2022
American Thoracic Society (ATS) 2022 International Conference
Publications & Abstracts
Systemic nanoparticle delivery of CRISPR-Cas9 ribonucleoproteins for effective tissue specific genome editing
June 26, 2020
Nature Communications
Selective organ targeting (SORT) nanoparticles for tissue-specific mRNA delivery and CRISPR–Cas gene editing
April 6, 2020
Nature Nanotechnology
Non-Viral CRISPR/Cas Gene Editing In Vitro and In Vivo Enabled by Synthetic Nanoparticle Co-Delivery of Cas9 mRNA and sgRNA
December 16, 2016
Wiley Online Library